When he was 6, Kavi lost his older brother to I-Cell (#Mucolipidosis II), a terminal #raredisease. Read what happen… https://t.co/ipLZiA58E8-5 hours 52 min ago
After two of her three children were diagnosed with GM1 (GM1 gangliosidosis), Marilee Leishman became active with t… https://t.co/ZmjIyRZPwm-1 day 7 hours ago
Our #RareBloodDisorder’s Head of Global Public Affairs, Simone Azevedo, enjoyed connecting with @ApmpsVIDA's, Regin… https://t.co/XvOZzVUI7S-1 day 20 hours ago